Revolutionizing Brain Health across Rare and Common Neurological Disorders

Voxel Therapeutics is pioneering novel therapeutic modalities to treat both rare and common neurological disorders, addressing some of the most urgent and intractable challenges in brain health.

Our mission is to begin where unmet need is greatest—rare neurological diseases—using an agnostic, precision-driven approach that applies right-sized gene and molecular tuning modalities tailored to each disorder. By co-developing therapies in close partnership with rare disease foundations, patient organizations, and academic leaders, we align discovery directly with patient biology and clinical reality.

Through these collaborative models, Voxel accelerates drug discovery, de-risks development, and advances toward durable, disease-modifying—and ultimately curative—therapies. What we learn in rare disease serves as the foundation for broader impact, enabling scalable solutions that extend to more prevalent neurological disorders.